The programme will contain scientific and strategic sessions in which the following issues will be discussed:

  • Research achievements in the field of neurodegenerative diseases, in particular lysosomal storage disorders (LSDs) at clinical and basic science level and in the field of Blood  Brain Barrier;
  • New recent advances on natural history and pathophysiology of LSDs;
  • Factors which control the entry into the brain of medicines and other therapeutic agents which may be helpful in treating central nervous system disease;
  • How B4B and the European Union might collaborate to stimulate interest on research in rare diseases,
  • The role of the industries in driving innovation for new therapeutic approaches for true unmet needs.